Link Found Between P. aeruginosa Infection and Disease Severity in CF Patients, Study Reports
Patients with cystic fibrosis (CF) whose lungs have never been colonized by the Pseudomonas aeruginosa bacterium have a milder form of...
Toddlers Age 1-2 With CF Can Now Be Treated With Kalydeco in Canada
Health Canada has approved the use of Kalydeco (ivacaftor) in toddlers age 1-2 years with certain genetic mutations that prevent the...
FDA puts Translate Bio’s rare disease mRNA drug on hold
The FDA has placed a clinical hold on the IND for Translate Bio’s mRNA treatment for ornithine transcarbamylase (OTC) deficiency, a...
Personalized Nutrition Programs May Help Improve Outcomes for CF Patients, Survey Suggests
New personalized strategies that can address the nutritional needs of cystic fibrosis patients may provide the best care and improve...
The Diverse Spectrum of Health Across the CF Community
If you’ve ever met more than one person with cystic fibrosis, it’s likely they had very different experiences than you. First, their...
At-home DNA test kits: Medical experts warn buyers beware
(WRIC) - Did you or someone you know get an at-home DNA test kit for Christmas? They were one of the hottest holiday items. It's an easy...
Cystic fibrosis drug combo found safe and effective for 2–5 year olds
An open label phase 3 study conducted at Ann & Robert H. Lurie Children’s Hospital of Chicago and other centers established that a...
Eluforsen Improves CFTR Protein Function in CF Patients with F508del Mutations, Phase 1 Trial Shows
An exploratory Phase 1 trial showed that repeated intranasal treatment with the therapy eluforsen improved CFTR protein activity in...
WHO Approves Ensifentrine as Name for Potential Inhaled Treatment Now in Clinical Trials
The World Health Organization (WHO) approved ensifentrine as the recommended name to identify the cystic fibrosis (CF) treatment...
