Triple Combo Treatment Improves Lung Function in Patients with Cystic Fibrosis
An investigational triple combination treatment regimen for cystic fibrosis (CF) improved patients’ lung function in 2 phase 3 studies,...
Ultrasound Predicts Advanced Liver Disease in CF Patients, According to Clinical Trial Data
Ultrasound may predict liver disease in young cystic fibrosis (CF) patients, according to the results of a clinical trial. Researchers...
Law Student returned to life with lung transplantation
Law student came back to life with lung transplantation, 20 years of law student struggles with genetic disease ISTANBUL – For many...
Worse CF Lung Outcomes Linked with Mutations Causing Iron Overload Disorder, Study Finds
Patients with cystic fibrosis (CF) who carry certain mutations in the HFE gene, which are also behind an iron overload disorder, have...
Proteostasis Therapeutics' Double and Triple-Combo CF Drugs Possible Threat to Vertex Dominance
Boston-based Proteostasis Therapeutics announced positive preliminary data from its ongoing Phase I clinical trial of PTI-808 and PTI-801...
FDA Approves AzurRx Biopharma Request to Test MS1819-SD in CF Patients with EPI
AzurRx BioPharma is planning a multi-center Phase 2 trial to be conducted in the United States and Europe to evaluate its lead candidate...
Chronic P. Aeruginosa Infection Greatly Raises Risk of Flares in Non-CF Bronchiectasis, Study Shows
People with non-cystic fibrosis (CF) bronchiectasis are at a significantly greater risk of exacerbations if they have chronic infections...
Vertex and Treating CF: 3 Disease-modifying Therapies Make Leap from Lab to Patients
Editor’s Note: This is the second of a four-part series looking at Vertex Pharmaceuticals and its “all in for CF” approach. Here, we...
Discovering the ancient origin of cystic fibrosis, the most common genetic disease in Caucasians
Imagine the thrill of discovery when more than 10 years of research on the origin of a common genetic disease, cystic fibrosis (CF),...
