Minimally Invasive Imaging Device Shows Changes in Nasal Airways, May Allow Earlier CF Diagnosis
A minimally invasive imaging device that generates high-resolution images of nasal airways, including the cilia and mucus, allows...
Proteostasis Begins Dosing in Phase 2 Trial of 3 CF Investigational Therapies
The first patient has been dosed in a Phase 2 clinical trial testing Proteostasis Therapeutics‘s combinations of three investigational...
Pregnancy in CF Women With Poor Lung Function Not Linked to Pulmonary Decline, Study Shows
Poorer lung function in pregnant women with cystic fibrosis (CF) is associated with a lower birth weight for offspring, and a higher...
Tezacaftor, Ivacaftor Combination Generally Safe, Well Tolerated in Children With CF Under Age 12
Data from a phase 3 trial are supporting the use of tezacaftor in combination with ivacaftor for the treatment of cystic fibrosis (CF) in...
Kalydeco’s Safety and Benefits Studied in CF Patients with Severe Lung Disease
Treatment with Kalydeco (ivacaftor) improved lung function, exercise capacity, and sweat chloride concentration in cystic fibrosis (CF)...
Specific Variables Improve Disease Severity Discrimination Among CF Transplant Candidates
The inclusion of Cystic Fibrosis Foundation Patient Registry variables in the lung allocation score (LAS) calculation allowed for...
Modified and More Rigorous Cleansing Procedure May Better Prepare CF Patients for Colonoscopy, Study
People with cystic fibrosis (CF) may require a modified and more rigorous cleansing procedure to prepare their bowels for a colonoscopy...
Ultrasound Can Help Detect Liver Disease in Kids with CF, Study Says
Ultrasound imaging can be a reliable diagnostic tool for early detection of liver disease in children with cystic fibrosis (CF), a study...
BillionToOne Announces Launch of UNITY Prenatal Screen
The diagnostics company BillionToOne has launched its first product for commercial and clinical use — a blood test designed to help...
‘Rare Barometer’ Program Helps Eurordis Shape EU Rare Disease Policy
People with rare diseases know that the right government policies can make a big difference in the quality of their own lives, and those...
