Specific Gene Mutation Causes Severe CF in Georgian Jewish Patients, Study Reports
The Q359K/T360K gene mutation, which is commonly found in Jewish patients of Georgian descent, is associated with a particularly severe...
Cystic Fibrosis Treatment Approved for Use in Children Aged 2 to 5 Years
Officials with the FDA have updated the label of lumacaftor/ivacaftor (Orkambi, Vertex Pharmaceuticals), approving the treatment's use in...
Vertex Pharma (VRTX) Receives European CHMP Positive Opinion for SYMKEVI for People with CF Aged 12
Vertex Pharmaceuticals (Europe) Limited (Nasdaq: VRTX), today announced that the European Medicines Agency’s (EMA) Committee for...
Gene Mutations Linked to Other Lung Diseases May Contribute to Bronchiectasis, Study Suggests
Mutations in genes linked to other lung diseases, specifically cystic fibrosis and primary ciliary dyskinesia, may also contribute to...
Vertex Anticipates Completing Enrollment of Phase 3 Trials Testing Triple Combo Therapies
Vertex Pharmaceuticals plans to conclude the enrollment of patients in its Phase 3 programs involving its triple combo therapies to treat...
CF Babies More Likely to be Born Preterm, Weigh Less, Study Finds
Babies with cystic fibrosis (CF) are more likely to be born preterm — less than 37 weeks of pregnancy — and have significantly lower...
Arcturus’ RNA Therapy for CF Shows Promise in Preclinical Studies, Company Announces
Arcturus Therapeutics’ RNA-based approach enables the production of healthy CFTR— the protein whose dysfunction is key in cystic fibrosis...
AIT’s Inhaled Nitric Oxide Shows Potential in Fighting Bacterial Infection Prevalent in CF Patients
Inhaled nitric oxide (NO) was shown to be an effective antibacterial agent against Mycobacterium abscessus infection in preclinical...
Cystic Fibrosis: Antioxidant-Enriched MVI May Decrease Respiratory Illnesses
MedicalResearch.com Interview with: Scott D Sagel MD PhD Professor of Pediatrics University of Colorado School of Medicine Aurora,...
New Method to Deliver Bacteria-killing Viruses Seen to Resolve Lung Infections in CF Mice
A new therapy which is administered directly into the lung of viruses can kill bacteria, and was shown to be effective in reducing...
