Phase 3 Trial of RDEB Therapy EB-101 to Start in 2019, Abeona Therapeutics Says
Abeona Therapeutics plans to start a Phase 3 trial in 2019 testing the cell therapy candidate EB-101 as a treatment for recessive...
People with Rare Diseases Are Humans, Not Commodities
If you keep up with CF research, you may have seen the news about Phase 3 of the triple combination Vertex therapies. In these results,...
Triple Combo Treatment Improves Lung Function in Patients with Cystic Fibrosis
An investigational triple combination treatment regimen for cystic fibrosis (CF) improved patients’ lung function in 2 phase 3 studies,...
NuvoAir Redefines Home Monitoring for Cystic Fibrosis Patients
STOCKHOLM--(BUSINESS WIRE)--Dec 4, 2018--THE FINDINGS from a pilot study into a new way of caring for those with cystic fibrosis (CF)...
Mucus Protects Lungs by Forming Layers, Preventing Worsening of Lung Diseases, Studies Reveal
Two new studies highlight the important role of mucus in cleaning and protecting the lungs, and how its accumulation and impaired...
Study Reveals How Cystic Fibrosis Affects Young Women’s Sexual Health
Girls with cystic fibrosis (CF) reach puberty six to eight months later than healthy girls, about 16 percent of young females with CF...
PARI Devices used in SHIP Study of Hypertonic Saline in Preschoolers with Cystic Fibrosis
MIDLOTHIAN, Va., Nov. 29, 2018 /PRNewswire/ -- A recent study in preschoolers with cystic fibrosis (CF) conducted by Cystic Fibrosis...
European Union Expands Kalydeco’s Approval to Certain CF Patients Ages 1-2
Kalydeco (ivacaftor) by Vertex Pharmaceuticals has been approved in the European Union for children ages 1-2 with cystic fibrosis (CF)...
Cystic Fibrosis Patients Exposed to Higher Risks of Liver Cancer
Researchers from Colorado, in the United States, shared the results of a study that showed that patients with cystic fibrosis would be at...
New Mucus Study Could Hold the Key to Clearing Your Phlegm
Mucus, you fickle fiend—usually, you’re there keeping us safe from whatever nasties sneak inside of us. But then you turn, becoming a...