AiCuris and Lysando Join Forces in the Fight Against Antimicrobial Resistance
Cooperation focused on the joint development and optimization of human anti-infective drug candidates against gram-negative and...
Hinge-like protein may open new doors in cystic fibrosis treatment
In recent decades, treatment options for people with cystic fibrosis have improved dramatically. The newest drugs, known as potentiators,...
Ultrasound Can Help Detect Liver Disease in Kids with CF, Study Says
Ultrasound imaging can be a reliable diagnostic tool for early detection of liver disease in children with cystic fibrosis (CF), a study...
Better Access to Relizorb for Patients on Feeding Tubes Advocated by Doctors and Dietitians
More than 60 cystic fibrosis experts strongly support Relizorb being made available to CF patients on tube feeding, pushing in a...
Hypertonic saline may be appropriate intervention for preschoolers with cystic fibrosis
New data from the SHIP study show that inhaled hypertonic saline, as compared with isotonic saline, improved lung clearance index in...
BillionToOne Announces Launch of UNITY Prenatal Screen
The diagnostics company BillionToOne has launched its first product for commercial and clinical use — a blood test designed to help...
FDA Grants Orphan Drug Status to AR-501, Potential CF Treatment for Chronic Lung Infections
AR-501, an investigational inhaled formulation of gallium citrate to treat chronic lung infections in patients with cystic fibrosis (CF),...
FDA Approves Symdeko for Treatment of CF Children, Ages 6 to 11, with Certain CFTR Mutations
The U.S. Food and Drug Administration (FDA) has approved Symdeko (tezacaftor/ivacaftor and ivacaftor) tablets for the treatment of...
‘Rare Barometer’ Program Helps Eurordis Shape EU Rare Disease Policy
People with rare diseases know that the right government policies can make a big difference in the quality of their own lives, and those...
Eluforsen Found to be Safe for Adults with Cystic Fibrosis Caused by F508del Mutation, Study Reports
The experimental treatment eluforsen is safe for adults with cystic fibrosis(CF) caused by a mutation called F508del, a new study...
