Kalydeco’s Efficacy Tied to Phosphorylation Levels of CFTR Protein, Study Suggests
CFTR channel activity is controlled by a molecular process known as phosphorylation. Now, a study suggests that the levels of...
New protein could offer a fresh target for cancer treatment
An international study in the Proceedings of the National Academy of Sciences shows a fascinating new drug target – a cell protein dubbed...
Eloxx Pharmaceuticals Announces Cystic Fibrosis Foundation (CF Foundation) To Provide Funding and Su
CF Foundation and Eloxx to form joint program advisory group focused on the development of ELX-02 for cystic fibrosis Eloxx plans to...
Safety, Early Effectiveness of POL6014 Confirmed in Phase 1 Trial
Single dosing of orally inhaled POL6014, an experimental therapy to treat chronic lung inflammation, can effectively block the activity...
Amikacin Liposome Therapy Has Similar Efficacy as Tobramycin for P. aeruginosa, Study Shows
Amikacin liposome inhalation suspension (ALIS) showed the same efficacy and similar safety profile as tobramycin inhalation solution...
National Study to Use Telehealth for Talk Therapy for CF Patients
Led by researchers at Drexel University, a national study will evaluate whether talk therapy delivered via telehealth can help people...
Cystic fibrosis carriers: What to know
A person who is a cystic fibrosis carrier has one copy of the gene for the condition. People need to have two copies of the gene to have...
Human pancreas on a chip can reveal more about disease
A researcher holds a dual-chamber chip that scientists used to bioengineer human pancreatic tissues to study the cause of Cystic...
Aridis Pharmaceuticals Reports Phase 2 Clinical Trial Results of AR-105 for the Treatment of Ventila
SAN JOSE, Calif., Sept. 3, 2019 /PRNewswire/ -- Aridis Pharmaceuticals, Inc. (Nasdaq: ARDS), a biopharmaceutical company focused on the...
FDA to Review Elexacaftor, Tezacaftor, Ivacaftor Combo for Cystic Fibrosis
The Food and Drug Administration (FDA) has accepted for priority review the New Drug Application (NDA) for elexacaftor (VX-445),...
